Our work is powered by a toolkit of five R&D approaches – two established platforms (chemistry and biotherapeutics) plus three advanced platforms (xRNA, radioligand therapy and gene and cell therapy) that will play an increasingly important role in making new medicines.
Chemistry is the discovery of low molecular weight synthetic molecules that can be optimized as medicines.
Biotherapeutics, or biologics, are medicines derived from the molecules of life, carefully engineered to treat specific diseases.
RNA therapies use various forms of ribonucleic acids (RNA) to modify biological pathways in the body to treat or cure specific illnesses.
Radioligand therapy delivers precision-targeted radiation to cancer cells in the body with the goal of limiting damage to surrounding tissue.
Gene and cell therapy
Gene therapies modify part of a patient’s genetic makeup to help treat genetic or inherited diseases. Cell therapies treat diseases by restoring or altering certain sets of cells or by using cells to carry a therapy through the body.