Cell and Gene Therapy

A scientist working in a laboratory at a Novartis location

Cell & Gene Therapy

We are reimagining medicine to power breakthrough innovation in cell and gene therapy

AveXis is now Novartis Gene Therapies

Novartis Gene Therapies is dedicated to developing and commercializing gene therapies for patients and families devastated by rare and life-threatening neurological genetic diseases.

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Cell & Gene Therapy Explained

What makes cell and gene therapy different from conventional medicine? Vox Creative helps explain.

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Delivering on the promise of cell and gene therapy for patients

New advances in cell and gene therapies offer the potential to transform medicine. They create an inflection point in our ability to treat and even potentially cure many intractable illnesses.

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Key focus areas

Currently, there are three key focus areas for development of transformative cell and gene therapies at Novartis: AAV-based therapies, CAR-T cell therapies and CRISPR-based technologies.

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CAR-T Cell Therapy and Beyond

Novartis is pioneering the way in the class of cell and gene treatment. This includes setting the standard in patient and caregiver support, safety and efficacy, access, and partnerships with healthcare institutions, local health authorities, and academic institutions around the world.

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Expanding CAR-T manufacturing in Europe

European Medicines Agency (EMA) recently approved two European Novartis sites for commercial CAR-T manufacturing.

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What is cell and gene therapy?

Scientific discoveries such as vaccines and antibiotics changed the course of history. Now cell and gene therapies are creating a new turning point in medicine and how we treat disease.

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A new era of medicine

Cell and gene therapies could help reduce or eliminate the need for treatments that need to be taken continuously, often for life.

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Collaborating to explore new gene regulation therapies

Novartis and Sangamo Therapeutics plan to pursue potential treatments for neurodevelopmental diseases.

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