 ##  [KPE179](/node/668026 "KPE179") 

  



del-zota

[Neuroscience](/taxonomy/term/2906)

[Phase 2](/taxonomy/term/2881)

[2026](/taxonomy/term/2821)

[PMO mediated exon 44 skipping](/taxonomy/term/12206)

 

Duchenne muscular dystrophy

[Lead Indication](/taxonomy/term/2811)



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